Mucopolysaccharidosis I - 101 Studies Found
Completed |
: Stem Cell Transplant w/Laronidase for Hurler :
: 2005-09-12 :
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Completed |
: A Study Investigating the Relationship Between the Development of Laronidase Antibody and Urinary GAG (Glycosaminoglycan) Levels in Aldurazyme® Treated Patients :
: 2017-04-24 : Other: This is an observational study This is an observational study |
Terminated |
: Study to Detect Unrecognized Mucopolysaccharidosis in Children Visiting Rheumatology, Hand or Skeletal Dysplasia Clinics :
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Completed |
: Iduronate-2-sulfatase Enzyme Replacement Therapy in Mucopolysaccharidosis II (MPS II) : Mucopolysaccharidosis II : 2003-09-29 :
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Completed |
: To Evaluate the Safety and Efficacy of GC1111 (Recombinant Human Iduronate-2-sulfatase) in Hunter Syndrome Patients : Mucopolysaccharidosis II : 2011-02-22 :
|
Not yet recruiting |
: Study of Idursulfase-beta (GC1111) in Hunter Syndrome : Mucopolysaccharidosis II : 2016-01-17 :
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Recruiting |
: Ascending Dose Study of Genome Editing by the Zinc Finger Nuclease (ZFN) Therapeutic SB-913 in Subjects With MPS II : Mucopolysaccharidosis II : 2017-01-13 : Biological: SB-913 Single dose of each of the 3 components of SB-913: ZFN1, ZFN2 and hIDS Donor |